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La Notizia


FDA approval of the Biologics License Application (BLA) for Waskyra, the first gene therapy for the treatment of Wiskott-Aldrich syndrome (WAS)
SITGEC would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community. The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for Waskyra , the first gene therapy for the treatment of Wiskott-Aldrich syn
10 dic 2025


2025 - Bambino Gesù Hospital, Rome
SITGEC's first standalone meeting took place in June, following on from the success of their inaugural conference in October 2024, which was held in collaboration with ESGCT. The 'Thematic Day on Broadening and Securing access to ATMPs' took place on 6th June at Bambino Gesù Children's Hospital in Rome.
23 giu 2025


EMBO Workshop titled “CRISPR-Cas: from biology to therapeutic applications” Sorrento
We would like to bring to your attention the upcoming EMBO Workshop titled “CRISPR-Cas: from biology to therapeutic applications”,...
23 mag 2025


Joint Postdoctoral Program at TIGEM and SR-Tiget
Fondazione Telethon launches a new training initiative for early-career scientists at its flagship Institutes Fondazione Telethon is a...
23 mag 2025


Group Leader position at SR-TIGET (Milan, Italy)
The San Raffaele Telethon Institute for Gene Therapy (SR-TIGET - www.sr-tiget.it ) is seeking tenure- track GROUP LEADERS wishing to...
23 mag 2025


2024 - Rome
The 31st ESGCT Annual Congress took place in collaboration with SITGEC on 22-25 October 2024 at La Nuvola in Rome. Fondazione Telethon...
12 feb 2025


Fondazione Telethon announces submission of MAA to EMA for Gene Therapy for the treatment of Wiskott-Aldrich Syndrome patients
Read the press release here for full details.
5 feb 2025


SITGEC 2024 Headline Numbers
See a summary of SITGEC's headline numbers from 2024.
6 gen 2025


School Event at the ESGCT and SITGEC 2024 Annual Congress
More than 1000 school students attended an event organised by Fondazione Telethon at the ESGCT/SITGEC Congress. Watch the event video here.
4 nov 2024
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