Foundation For Rare Diseases (Fondation Maladies Rares, France) organises an online MOOC on gene and gene-based cell therapies for rare diseases .     Foundation For Rare Diseases (Fondation Maladies Rares, France) organises an online MOOC on gene and gene-based cell therapies for rare diseases .   The course features contributions from leading U.S. and European researchers — including Alain Fischer, Heather Gray Edwards, Alessio Cantore, Zoltan Ivics, Sylvie Odent, Salima Ha

SITGEC è profondamente addolorata per la scomparsa del Professor Claudio Bordignon.

SITGEC would like to congratulate Fondazione Telethon and HSR-TIGET on the milestone achievement of the FDA approval of WAS ex vivo gene therapy. Please see below their statement: We are honoured to share a moment of profound significance for us, for patients, families, and the scientific community.    The U.S. Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for  Waskyra , the  first gene therapy for the treatment of Wiskott-Aldrich syn

We would like to bring to your attention the upcoming  EMBO Workshop  titled “CRISPR-Cas: from biology to therapeutic applications”,...

Read the press release here for full details.

See a summary of SITGEC's headline numbers from 2024.

More than 1000 school students attended an event organised by Fondazione Telethon at the ESGCT/SITGEC Congress. Watch the event video here.